CFTR Modulator Therapies
CFTR Modulator Therapies
Aug 13, 2024
cff.org
Types of CFTR Mutations
Types of CFTR Mutations
Oct 16, 2024
cff.org
The journey to end cystic fibrosis isn’t a straight line. It’s an evolving map with many paths and unique challenges. That’s why we’re pursuing several different approaches to help achieve our goal of restoring CFTR protein and function in 100 percent of people living with cystic fibrosis. Dr. Bill Skach, EVP and Chief Scientific Officer at the Foundation, discusses how genetic-based therapies such as mRNA therapy, DNA therapy or gene therapy, and gene editing, could allow normal CFTR protein to
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