Despite innovative new research, many cell and gene therapies do not make it all the way to the patients. Researchers and ...
Scientists developed a charge-free polymer-DNA complex that boosts cellular DNA uptake 14-fold in mice, avoiding the harmful ...
Daphne O. Martschenko and Sam Trejo both want to make the world a better, fairer, more equitable place. But they disagree on ...
Genetic medicine is rapidly transforming the landscape of cancer research, offering novel strategies for treating malignancies beyond the capabilities of ...
One of the most promising is its cardiovascular disease therapy candidate CTX310, a single-treatment gene therapy that has ...
Health systems learn why cell and gene therapy success depends on workflows, staffing, and finances—not just science—and how to build them.
Henry Ford Health has treated the first Michigan patient outside clinical trials with Roctavian, the newly approved gene ...
My son, who’s almost 3, is asymptomatic and thriving. His syndrome mostly just means annual visits to a C.F. clinic for monitoring. But for future pregnancies, we are debating whether we should do I.V ...
A gene therapy that patients breathe in has been found to shrink lung tumours by inserting immune-boosting genes into ...
Even when promising clinical trials exist, and the FDA allows expanded access, rare disease patients like my granddaughter ...
2025 was a rollercoaster year for the cell and gene therapy field. Stories such as the successful treatment of ‘Baby KJ’ using a bespoke gene editor developed through a public–private partnership, and ...
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