A Plymouth mother is marking what would have been her son’s 12th birthday by honoring his life.

The singer’s 14-month-old daughters were diagnosed with SMA Type 1, a severe condition affecting muscle strength and ...

A recent Harvard study introduces a new method for treating spinal muscular atrophy. The study used "base editing" to target the disease's root cause by modifying the survival motor neuron gene. For ...

As August marks SMA Awareness Month, Cure SMA is drawing attention to its 2025 State of SMA report, an annual data resource ...

Scholar Rock (NASDAQ: SRRK), a global biopharmaceutical company dedicated to improving the lives of patients with rare, severe, and debilitating neuromuscular diseases by applying its world-leading ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 currently approved disease-modifying therapies that restore SMN protein ...

Spinal muscular atrophy is a progressive neurodegenerative disease that affects the central nervous system, peripheral nervous system and voluntary muscle movement, according to the Muscular Dystrophy ...

You might not think of diabetes when you think of muscle function. But a common diabetes drug that regulates blood sugar can also prevent muscle atrophy and muscular fibrosis—which can help the ...

Researchers from Tokyo Metropolitan University have developed a way to treat aging-related muscular atrophy using regenerative medicine. Conventional methods to implant myoblasts, precursors to muscle ...