Forbes

From Research To Reality: Gene Therapy For Metachromatic Leukodystrophy

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...
BlackDoctor.org

Lymphatic Drainage Massage: Benefits, Risks, and What to Expect

Lymphatic drainage massage gently moves lymph fluid to reduce swelling, support recovery, and improve circulation. Learn ...
The Healthy @Reader's Digest on MSN

I’m a regenerative medicine MD.—here’s the only lymphatic drainage product I use, and it’s under $60

Among jade rollers, gua sha, dry brushes and more, this doctor leans on clinical science to employ a de-puffing method supported by data.
MedCity News

Gene Therapy Is Now First FDA-Approved Treatment for Rare & Fatal CNS Disorder

A genetic medicine at the heart of a $387 million Kyowa Kirin acquisition has won FDA approval, a regulatory decision that makes the one-time treatment the first approved therapy for the rare ...
Nasdaq

FDA Approves First Gene Therapy For Kids With Early-onset MLD

(RTTNews) - The U.S. Food and Drug Administration approved Lenmeldy (atidarsagene autotemcel) gene therapy to treat children with early-onset metachromatic leukodystrophy or MLD. Lenmeldy, formerly ...
Medical News Today

How a gene therapy cures infants with fatal genetic disease MLD

Share on Pinterest Scientists have managed to create a treatment for the rare genetic disorder MLD. smolaw11/Getty Images Doctors in the United Kingdom have used a revolutionary gene therapy to cure a ...
Nasdaq

Homology Medicines Presents Data from Investigational PKU and MLD Gene Therapy Programs that Demonstrate Preclinical Proof-of-Concept for Potential One-Time Therapies

BEDFORD, Mass., Oct. 21, 2019 (GLOBE NEWSWIRE) -- Homology Medicines, Inc. (Nasdaq: FIXX), a genetic medicines company, announced today the presentation of preclinical data that support its ...
WSIL-TV

A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access

(CNN) — A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the world ...
Medscape

FDA OKs First Gene Therapy for Metachromatic Leukodystrophy

The US Food and Drug Administration (FDA) has approved the first gene therapy for metachromatic leukodystrophy (MLD), a rare and debilitating genetic disease affecting the brain and nervous system.
Monthly Prescribing Reference

Gene Therapy Candidate Gets Priority Review for Metachromatic Leukodystrophy

Credit: Shutterstock. OTL-200 is an ex vivo autologous hematopoietic stem cell gene therapy. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License Application ...
WRAL

A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access

(CNN) — A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the world ...