Duchenne therapy may be evolving from slowing disease to reversing it—with RNA approaches offering the prospect of restoring ...
Editor’s note: This is an automatically generated transcript. Please notify [email protected] if there are concerns regarding accuracy of the transcription. One key aspect of the journey for a person ...
MISSISSAUGA, ON, Oct. 2, 2025 /CNW/ - Kye Pharmaceuticals ("Kye") announced today that Health Canada has approved AGAMREE® (vamorolone) for the treatment of Duchenne Muscular Dystrophy (DMD) in boys a ...
Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the deterioration of skeletal muscle in the disease. The use of ...
Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying therapies using gene replacement, antisense oligonucleotides, and gene transfer ...
Every movement we make, whether walking, speaking or even breathing, depends on the health of our muscles and nerves. For people living with one of the more than 300 rare conditions known as ...
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