In a setback for Sarepta Therapeutics, a New York panel has voted unanimously to recommend the state Medicaid program pause ...

Long-term treatment with givinostat in boys with Duchenne muscular dystrophy continues to show a favourable safety and tolerability profile ...

Sarepta prepares to present new data on Duchenne and limb-girdle muscular dystrophy gene therapy programs this week.

Approximately 16 boys with Duchenne Muscular Dystrophy (DMD), including several teenagers, are set to benefit from the drug, ...

Duchenne therapy may be evolving from slowing disease to reversing it—with RNA approaches offering the prospect of restoring ...

One of those things is the CureDuchenne clinic in Denton. It provides care to underserved and uninsured people with Duchenne.

Health Canada has approved Santhera Pharmaceuticals’ Agamree (vamorolone) to treat Duchenne muscular dystrophy (DMD) in ...

SonoThera™, a biotechnology company dedicated to treating the root cause of human diseases by developing the next generation ...

While it’s established that Duchenne muscular dystrophy (DMD) causes a loss of muscle mass and strength, few studies have examined the gastrointestinal issues tied to DMD. Initial fractures are the ...

A custom-built racetrack is allowing a 9-year-old with Duchenne Muscular Dystrophy to enjoy recess at Linda Vista Elementary using his wheelchair.

Chad Williams, who has muscle-wasting condition Duchenne muscular dystrophy, runs the Villa4Ever podcast that he says is ...

STATEN ISLAND, N.Y. — Those who participated in “The 13th annual Michael 2025 Step For A Cure 5k Run And Walk” at the FDR ...