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Yu: We have so many opportunities, not only treating rare diseases with AAV but also many common diseases like diabetes, Alzheimer’s, aging, and even COVID-19. Replacing the gene of interest and ...

AAV Vectors AAVs are single-stranded DNA viruses that require co-infection with other viruses, mainly adenoviruses, to replicate. When used as gene therapy vehicles, researchers generate recombinant ...

Biotech Vertex discontinues AAV research for gene therapies By Darren Incorvaia May 2, 2025 6:22pm Vertex Pharmaceuticals Adenovirus Cell & Gene Therapy viral vectors ...